Growth and Development-related Outcomes in Children With Transfusion-dependent Beta-thalassemia After Gene Therapy

RecruitingOBSERVATIONAL
Enrollment

100

Participants

Timeline

Start Date

June 5, 2023

Primary Completion Date

December 31, 2028

Study Completion Date

December 31, 2029

Conditions
Transfusion-dependent Beta-ThalassemiaGene Therapy
Interventions
GENETIC

Gene therapy

Autologous edited hematopoietic stem cell transplantation

Trial Locations (1)

Unknown

RECRUITING

Regenerative Medicine Center, Tianjin

All Listed Sponsors
lead

Institute of Hematology & Blood Diseases Hospital, China

OTHER