ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisis

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

21

Participants

Timeline

Start Date

August 22, 2023

Primary Completion Date

October 31, 2025

Study Completion Date

October 31, 2029

Conditions
X-linked Retinoschisis
Interventions
BIOLOGICAL

ATSN-201

AAV.SPR-hGRK1-hRS1syn

Trial Locations (4)

19104

RECRUITING

Children's Hospital of Philadelphia, Philadelphia

33136

RECRUITING

Bascom Palmer Eye Institute, Miami

90027

RECRUITING

Children's Hospital of Los Angeles, Los Angeles

97239

RECRUITING

Oregon Health Sciences University, Portland

Sponsors
All Listed Sponsors
lead

Atsena Therapeutics Inc.

INDUSTRY