30
Participants
Start Date
November 10, 2024
Primary Completion Date
July 30, 2027
Study Completion Date
November 1, 2027
NOT_YET_RECRUITING
The University of Texas Southwestern Medical Center, Dallas
RECRUITING
Hospices Civils De Lyon, Bron
Lead Sponsor
Vaincres Les Maladies Lysosomales
UNKNOWN
Association Sanfilippo Sud
UNKNOWN
Aparito Ltd.
INDUSTRY
Phoenix Nest
INDUSTRY