Natural History Study of Participants With Sanfilippo Syndrome Type IIIC

RecruitingOBSERVATIONAL
Enrollment

30

Participants

Timeline

Start Date

November 10, 2024

Primary Completion Date

July 30, 2027

Study Completion Date

November 1, 2027

Conditions
Sanfilippo Syndrome Type C
Trial Locations (2)

75390

NOT_YET_RECRUITING

The University of Texas Southwestern Medical Center, Dallas

690007539

RECRUITING

Hospices Civils De Lyon, Bron

Sponsors

Lead Sponsor

All Listed Sponsors
collaborator

Vaincres Les Maladies Lysosomales

UNKNOWN

collaborator

Association Sanfilippo Sud

UNKNOWN

collaborator

Aparito Ltd.

INDUSTRY

lead

Phoenix Nest

INDUSTRY

NCT05825131 - Natural History Study of Participants With Sanfilippo Syndrome Type IIIC | Biotech Hunter | Biotech Hunter