Orphan Drugs for Inherited Metabolic Diseases

CompletedOBSERVATIONAL
Enrollment

39

Participants

Timeline

Start Date

October 1, 2022

Primary Completion Date

May 1, 2024

Study Completion Date

October 1, 2024

Conditions
Inborn Errors of Metabolism
Trial Locations (1)

1011

Lausanne University Hospital, Lausanne

All Listed Sponsors
lead

University of Lausanne

OTHER