Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy

PHASE2RecruitingINTERVENTIONAL
Enrollment

54

Participants

Timeline

Start Date

September 21, 2023

Primary Completion Date

January 31, 2026

Study Completion Date

January 31, 2026

Conditions
Spinal Muscular Atrophy
Interventions
DRUG

NMD670

Tablets

DRUG

Placebo

Tablets

Trial Locations (29)

27278

RECRUITING

Rare Disease Research - Raleigh-Durham, Hillsborough

30329

WITHDRAWN

Rare Disease Center, Atlanta

32608

RECRUITING

UF Fixel Institute for Neurological Diseases, Gainesville

43210

RECRUITING

The Ohio State University Wexner Medical Center, Columbus

63110

RECRUITING

Washington University School of Medicine, St Louis

65212

RECRUITING

Roy Blunt NextGen Precision Health Institute, Columbia

66160

RECRUITING

University of Kansas Medical Center, Kansas City

76208

RECRUITING

Neurology Rare Disease Center, Denton

90095

RECRUITING

UCLA David Geffen School Of Medicine - Neurology, Los Angeles

94304

RECRUITING

Stanford University Medical Center, Palo Alto

Unknown

RECRUITING

UZ Leuven - Neurochirurgie Campus Gasthuisberg, Leuven

RECRUITING

CHR de la Citadelle - Neurologie, Liège

RECRUITING

Heritage Medical Research Clinic, Calgary

RECRUITING

Genge Partners Inc., Montreal

RECRUITING

Aarhus Universitetshospital, Neurologisk Afdeling, Aarhus

RECRUITING

Rigshospitalet - Neurologisk Afdeling, Copenhagen

RECRUITING

Charite - Campus Virchow-Klinikum (CVK), Berlin

RECRUITING

Universitätsklinikum Essen - Klinik Für Neurologie, Essen

RECRUITING

Istituto Giannina Gaslini, IRCCS, Genova

RECRUITING

Istituto Neurologico C. Besta, Fondazione IRCCS, Milan

RECRUITING

Ospedale Niguarda, ASST Grande Ospedale Metropolitano Niguarda, Milan

RECRUITING

Università degli studi di Pisa, Pisa

RECRUITING

PU A. Gemelli, Università Cattolica del Sacro Cuore, Roma

RECRUITING

AOU Città della Salute e della Scienza di Torino, Torino

RECRUITING

Universitair Medisch Centrum Utrecht, locatie Academisch Zie - Neurology, Utrecht

RECRUITING

Hospital Universitari Vall D Hebron, Barcelona

RECRUITING

H. Donostia, Donostia / San Sebastian

RECRUITING

Hospital Materno Infantil La Paz, Madrid

RECRUITING

Hospital Universitario y Politécnico La Fe, Valencia

Sponsors

Lead Sponsor

All Listed Sponsors
lead

NMD Pharma A/S

INDUSTRY

NCT05794139 - Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy | Biotech Hunter | Biotech Hunter