Mucolipidosis Type IV Natural History Study

RecruitingOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

March 15, 2023

Primary Completion Date

March 31, 2026

Study Completion Date

March 31, 2026

Conditions
Mucolipidosis Type IV
Trial Locations (1)

02144

RECRUITING

Massachusetts General Hospital, Boston

All Listed Sponsors
lead

Massachusetts General Hospital

OTHER