A Study to Provide Continued Access to Mitapivat for Participants Who Previously Completed an Agios-Sponsored Mitapivat Study

PHASE4Enrolling by invitationINTERVENTIONAL
Enrollment

6

Participants

Timeline

Start Date

July 6, 2023

Primary Completion Date

August 31, 2029

Study Completion Date

August 31, 2029

Conditions
Pyruvate Kinase DeficiencyAnemia, Hemolytic
Interventions
DRUG

Mitapivat

Tablets

Trial Locations (4)

L8S3Z5

McMaster Centre for Transfusion Medicine McMaster University, Hamilton

980-8574

Tohoku University Hospital, Sendai

615-8256

Kyoto Katsura Hospital, Kyoto

143-8541

Toho University - Omori Medical Center, Ōta-ku

Sponsors
All Listed Sponsors
lead

Agios Pharmaceuticals, Inc.

INDUSTRY