Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments

RecruitingOBSERVATIONAL
Enrollment

500

Participants

Timeline

Start Date

November 28, 2022

Primary Completion Date

November 27, 2027

Study Completion Date

November 27, 2027

Conditions
Spinal Muscular Atrophy
Trial Locations (5)

Unknown

RECRUITING

Istituto Gaslini, Genova

RECRUITING

Nemo Sud, Messina

RECRUITING

Centro Clinico nemo, Milan

RECRUITING

Ospedale Bambino gesu, Rome

RECRUITING

Policlinico gemelli, Rome

All Listed Sponsors
collaborator

University of Milan

OTHER

collaborator

Bambino Gesù Hospital and Research Institute

OTHER

collaborator

University of Messina

OTHER

collaborator

Gaslini Children's Hospital

OTHER

lead

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

OTHER