NCT05765981View on ClinicalTrials.gov

An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.

EARLY_PHASE1RecruitingINTERVENTIONAL
Enrollment

6

Participants

Timeline

Start Date

January 30, 2023

Primary Completion Date

February 20, 2025

Study Completion Date

February 20, 2029

Conditions
Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
Interventions
DRUG

VGN-R09b

VGN-R09b will be injected into bilateral putamen by stereotactic surgery.（Through the SmartFlow Ventricular Cannula or the parenchymal injection tube actually used in the research center）

Trial Locations (1)

200127

RECRUITING

Shanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine, Shanghai

All Listed Sponsors
collaborator

Shanghai Vitalgen BioPharma Co., Ltd.

INDUSTRY

lead

Shanghai Jiao Tong University School of Medicine

OTHER