A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works

PHASE3RecruitingINTERVENTIONAL
Enrollment

202

Participants

Timeline

Start Date

March 7, 2023

Primary Completion Date

February 26, 2029

Study Completion Date

February 26, 2029

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
DRUG

Pozelimab

Administered per the protocol

DRUG

Cemdisiran

Administered per the protocol

Trial Locations (37)

114

RECRUITING

Tri-Service General Hospital, Taipei

1083

RECRUITING

Semmelweis University/Semmelweis Egyetem, Budapest

1634

RECRUITING

St Lukes Medical Center, Quezon City

10002

RECRUITING

National Taiwan University Hospital, Taipei

10126

RECRUITING

SC Hematology, AOU Città della Salute e della Scienza di Torino, Torino

10330

RECRUITING

King Chulalongkorn Memorial Hospital, Bangkok

11942

RECRUITING

Jordan University Hospital (JUH), Amman

15072

RECRUITING

Clinica San Felipe, Lima

16247

RECRUITING

St. Vincent Hospital, Suwon

16499

RECRUITING

Ajou University Medical Center, Suwon

25200

RECRUITING

Hospital Tg Ampuan Afzan, Kuantan

33305

RECRUITING

Chang Gung Memorial Hospital - Linkou Branch, Taoyuan District

35100

RECRUITING

Ege University Faculty of Medicine, Bornova

40002

RECRUITING

Srinagarind Hospital, Khon Kaen

40447

RECRUITING

China Medical University Hospital, Taichung

48013

RECRUITING

Hospital Universitario Basurto, Bilbao

49241

RECRUITING

Pusan National University Hospital, Busan

50139

RECRUITING

Aou Careggi, Florence

50200

RECRUITING

Chiang Mai University, Chiang Mai

68000

RECRUITING

Hospital Ampang, Ampang

88200

RECRUITING

Hospital Queen Elizabeth, Kota Kinabalu

90110

RECRUITING

Prince Of Songkla Hospital, Prince Of Songkhla University, Hat Yai

97002

RECRUITING

Hualien Tzu Chi Hospital, Hualien City

110085

RECRUITING

Rajiv Gandhi Cancer Institute & Research Center (RGCIRC) - Rohini Campus, New Delhi

119074

RECRUITING

National University Hospital, Singapore

302017

RECRUITING

Bhagwan Mahaveer Cancer Hospital and Research Centre (BMCHRC), Jaipur

400015

RECRUITING

Prof Dr Ion Chiricuta Cancer Institute, Cluj-Napoca

682041

RECRUITING

Amrita Institute of Medical Sciences (AIMS) and Research Centre Aims, Kochi

M5G 2C4

RECRUITING

Toronto General Hospital, Toronto

305-8576

RECRUITING

University of Tsukuba Hospital, Tsukuba

85-168

RECRUITING

Szpital Uniwersytecki Nr2 Bydgoszcz, Bydgoszcz

405-760

RECRUITING

Gachon University Gil Medical Center, Incheon

03722

RECRUITING

Severance Hospital Yonsei University Health System, Seoul

06351

RECRUITING

Samsung Medical Center, Seoul

07985

RECRUITING

Ewha Womans University Mokdong Hospital, Seoul

08036

RECRUITING

Hospital Clinic de Barcelona, Barcelona

LS97TF

RECRUITING

Leeds Teaching Hospitals NHS Trust - St. James Institute of Oncology, Leeds

All Listed Sponsors
lead

Regeneron Pharmaceuticals

INDUSTRY