Gene Editing as a Therapeutic Approach for Rett Syndrome

RecruitingOBSERVATIONAL
Enrollment

40

Participants

Timeline

Start Date

March 1, 2021

Primary Completion Date

November 1, 2025

Study Completion Date

March 1, 2026

Conditions
Rett Syndrome
Interventions
OTHER

Gene editing in vitro

Testing of gene editing efficiency in vitro in human cellular models derived from patients

Trial Locations (1)

53100

RECRUITING

University of Siena, Siena

All Listed Sponsors
lead

University of Siena

OTHER