125
Participants
Start Date
March 27, 2023
Primary Completion Date
May 20, 2024
Study Completion Date
May 24, 2024
No Intervention
As this is an observational study, no intervention will be administered.
Fundación Española para el Estudio y Tratamiento de la Enfermedad de Gaucher (FEETEG), Zaragoza
Lead Sponsor
Takeda
INDUSTRY