301
Participants
Start Date
February 3, 2023
Primary Completion Date
May 31, 2026
Study Completion Date
April 1, 2027
Tominersen 60 mg
60 mg tominersen administered intrathecally every 16 weeks (Q16W).
Placebo
Matching placebo administered intrathecally Q16W.
Tominersen 100 mg
100 mg tominersen administered intrathecally Q16W.
Rigshospitalet, Hukommelsesklinikken, København Ø
Royal Melbourne Hospital, Parkville
Neurozentrum Siloah, Gümligen
Monash Medical Centre, Clayton
Waikato Hospital, Hamilton
Universitätsspital Basel, Basel
Perron Institute for Neurological and Translational Science, Nedlands
Uniklinik fuer Neurologie, Medizinische Universitaet Innsbruck, Innsbruck
New Zealand Brain Research Institute, Christchurch
Charité - Universitätsmed. Berlin, Klinik für Psychiatrie und Psychotherapie, Berlin
CHU de la Timone - Hopital d Adultes, Marseille
Dent Neurological Institute, Amherst
University of Pittsburgh, Pittsburgh
Georgetown University, Washington D.C.
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan
John Hopkins University School of Medicine, Baltimore
Universitätsklinikum Schleswig-Holstein / Campus Lübeck, Lübeck
Hospital Ramon y Cajal, Madrid
CHU toulouse - Hôpital Purpan, Toulouse
University of Florida, Gainesville
Groupe Hospitalier Pellegrin, Bordeaux
University of South Florida, Tampa
Hopital Gui de Chauliac, Montpellier
Uab Medicine, Birmingham
Vanderbilt University Medical Center, Nashville
Ospedale Bellaria, Bologna
Hospital Universitario Virgen Macarena, Seville
St. Josef-Hospital, Neurologische Klinik der Ruhr-Uni, Bochum
Hospital Universitario la Fe, Valencia
Henry Ford Hospital, Detroit
Hospital de Cruces, Barakaldo
CHU Angers, Batiement Larrey 2, Neurologie, Angers
Uniklinik RWTH Aachen, Aachen
University of Iowa Hospitals and Clinics, Iowa City
German Center for Neurodegenerative Diseases (DZNE), Bonn
Northwestern University, Chicago
CHU Strasbourg Hpital Hautepierre, Strasbourg
The University of Texas Health Science Center at Houston, Houston
CenExel Rocky Mountain Clinical Research, LLC, Englewood
kbo - Isar-Amper-Klinikum Taufkirchen, Taufkirchen
Barrow Neurological Institute, Phoenix
Universitätsklinikum Ulm, Ulm
Universitätsklinikum Erlangen, Abteilung Molekulare Neurologie, Erlangen
Hopital Henri Mondor, Créteil
University of California Davis Medical System, Sacramento
EvergreenHealth Investigational Drug Services, Kirkland
Inland Northwest Research, Spokane
Beth Israel Deaconess Medical Center, Boston
CINME, Buenos Aires
Hospital Ramos Mejía, CABA
INEBA, Capital Federal
Hospital Britanico de Buenos Aires, Ciudad Autonoma Buenos Aires
University of Alberta Hospital, Edmonton
Montreal Neurological Inst, Montreal
Hopital Roger Salengro Service de Neurologie, Lille
Azienda Ospedaliera Sant'Andrea, Rome
Szpital Sw. Wojciecha, Gdansk
Krakowska Akademia Neurologii Sp z o.o. Centrum Neurologii K, Krakow
Wojskowy Instytut Medycyny Lotniczej, Warsaw
Hospital de Santa Maria, Lisbon
CNS - Campus Neurológico, Torres Vedras
Hospital Universitario de Badajoz, Badajoz
Hospital de la Santa Creu i Sant Pau, Barcelona
Hospital Universitario de Burgos. Servicio de Neurología, Burgos
University Hospitals Birmingham NHS Foundation Trust, Birmingham
Addenbrookes Hospital, Cambridge
Chapel Allerton Hospital, Leeds
UCL Hospital NHS Trust, London
John Radcliffe Hospital, Oxford
Southampton University Hospitals NHS Trust, Southampton
Hoffmann-La Roche
INDUSTRY