Study of AOC 1044 in Healthy Adult Volunteers and Participants With Duchenne Muscular Dystrophy (DMD) Mutations Amenable to Exon 44 Skipping

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

70

Participants

Timeline

Start Date

November 9, 2022

Primary Completion Date

November 25, 2024

Study Completion Date

November 25, 2024

Conditions
Duchenne Muscular DystrophyExon 44
Interventions
DRUG

AOC 1044

AOC 1044 will be administered via intravenous (IV) infusion

DRUG

Placebo

Placebo will be administered via intravenous (IV) infusion.

Trial Locations (10)

27278

Rare Disease Research NC, Hillsborough

30329

Rare Disease Research - Atlanta, Atlanta

43215

Abigail Research Institute at Nationwide Children's Hospital, Columbus

52242

University of Iowa, Iowa City

55101

Gillette Children's, Saint Paul

72202

Arkansas Children's, Little Rock

78217

Worldwide Clinical Trials (Part A only), San Antonio

92037

UCSD, La Jolla

94304

Stanford University, Palo Alto

01655

University of Massachusetts Chan Medical School, Worcester

Sponsors
All Listed Sponsors
lead

Avidity Biosciences, Inc.

INDUSTRY