70
Participants
Start Date
November 9, 2022
Primary Completion Date
November 25, 2024
Study Completion Date
November 25, 2024
AOC 1044
AOC 1044 will be administered via intravenous (IV) infusion
Placebo
Placebo will be administered via intravenous (IV) infusion.
Rare Disease Research NC, Hillsborough
Rare Disease Research - Atlanta, Atlanta
Abigail Research Institute at Nationwide Children's Hospital, Columbus
University of Iowa, Iowa City
Gillette Children's, Saint Paul
Arkansas Children's, Little Rock
Worldwide Clinical Trials (Part A only), San Antonio
UCSD, La Jolla
Stanford University, Palo Alto
University of Massachusetts Chan Medical School, Worcester
Lead Sponsor
Avidity Biosciences, Inc.
INDUSTRY