Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

RecruitingOBSERVATIONAL
Enrollment

32

Participants

Timeline

Start Date

October 3, 2022

Primary Completion Date

March 31, 2029

Study Completion Date

March 31, 2029

Conditions
Pelizaeus-Merzbacher Disease
Trial Locations (4)

94270

RECRUITING

Ionis Investigative Site, Le Kremlin-Bicêtre

Unknown

RECRUITING

Ionis Investigative Site, Clermont-Ferrand

RECRUITING

Ionis Investigative Site, Göttingen

1081 HV

RECRUITING

Ionis Investigative Site, Amsterdam

Sponsors
All Listed Sponsors
lead

Ionis Pharmaceuticals, Inc.

INDUSTRY