A Natural History Study of Sanfilippo Syndrome Type D

CompletedOBSERVATIONAL
Enrollment

10

Participants

Timeline

Start Date

January 22, 2023

Primary Completion Date

November 1, 2024

Study Completion Date

November 1, 2024

Conditions
Sanfilippo Syndrome Type D
Trial Locations (1)

10032

Columbia University Irving Medical Center, New York

Sponsors

Lead Sponsor

All Listed Sponsors
collaborator

National Institute of Neurological Disorders and Stroke (NINDS)

NIH

lead

Phoenix Nest

INDUSTRY

NCT05648851 - A Natural History Study of Sanfilippo Syndrome Type D | Biotech Hunter | Biotech Hunter