A Study to Evaluate the Efficacy and Safety of Obinutuzumab Versus MMF in Participants With Childhood Onset Idiopathic Nephrotic Syndrome

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

85

Participants

Timeline

Start Date

March 29, 2023

Primary Completion Date

September 4, 2025

Study Completion Date

September 4, 2026

Conditions
Childhood Idiopathic Nephrotic Syndrome
Interventions
DRUG

Obinutuzumab

Obinutuzumab will be administered as per schedule specified in the respective arm.

DRUG

MMF

MMF will be administered as per schedule specified in the respective arm.

DRUG

Prednisone

Participants taking prednisone or equivalent at randomization will follow a guided tapering schedule to reach the goal of 0mg/day by Weeks 4-6 (and no later than Week 8 following randomization and continue without prednisone through Week 52.

DRUG

Methylprednisolone

Methylprednisolone 80 mg (or 1.5 mg/kg if \</=45 kg) IV will be administered as premedication prior to infusions.

DRUG

Acetaminophen/ Paracetamol

Acetaminophen 15 mg/kg (maximum dose 1000 mg) will be administered PO as premedication prior to infusions.

DRUG

Diphenhydramine Hydrochloride

Diphenhydramine HCl 0.5-1 mg/kg (maximum dose 50 mg) will be administered PO or IV as premedication prior to infusions.

Trial Locations (55)

1090

Hôpital Universitaire des Enfants Reine Fabiola, Brussels

9000

UZ Gent, Ghent

10126

Ospedale Infantile Regina Margherita - INCIPIT - PIN, Turin

16147

Istituto G Gaslini Ospedale Pediatrico IRCCS - INCIPIT - PIN, Genoa

20010

Children's National Hospital, Washington D.C.

20122

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico - Clinica De Marchi - INCIPIT - PIN, Milan

22903

University of Virginia Health System, Charlottesville

27710

Duke University Health Systems, Durham

32827

Nemours Children's Hospital, Orlando

33021

Memorial Healthcare System, Hollywood

33612

University of South Florida, Tampa

34295

CHU Montpellier- Hopital Arnaud de VIlleneuve, Montpellier

39008

Hospital Universitario Marques de Valdecilla, Santander

45010

Celal Bayar University Medical Faculty, Manisa

48903

Hospital Universitario Cruces, Barakaldo

69500

Chu Toulouse, Bron

Hopital Femme Mere Enfants, Bron

75015

Hopital Necker - Enfants Malades, Paris

75019

Hopital Robert Debre, Paris

90048

Cedars Sinai Medical Center, Los Angeles

94010

Hopital Henri Mondor, Créteil

94304

Lucile Packard Children's Hospital - Stanford, Palo Alto

100034

Peking University First Hospital, Beijing

310003

The children's hospital , Zhejiang university school of medicine, Hangzhou

430030

Tongji Hosp, Tongji Med. Col, Huazhong Univ. of Sci. & Tech, Wuhan

450018

Henan Children's Hospital Zhengzhou Children's Hospital, Zhengzhou

510080

The First Affiliated Hospital of Sun Yat-sen University, Guangzhou

710003

Xi'an Children's Hospital, Xi'an

1838561

Tokyo Metropolitan Children's Medical Center, Tokyo

6500047

Hyogo prefectural Kobe Children's Hospital, Hyogoken

94143-2350

University of California Benioff Children's Hospital, San Francisco

33155-3009

Nicklaus Children's Hospital, Miami

30329-2309

Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta

48109-0934

University of Michigan, Ann Arbor

07601

Hackensack University Medical Center, Hackensack

27514-2286

UNC Hospitals Outpatient Center at Eastowne, Chapel Hill

28203-5866

Levine Children's Hospital, Charlotte

84113-1103

University of Utah - Primary Children's Hospital - PPDS, Salt Lake City

99010-120

Instituto Méderi de Pesquisa e Saúde, Passo Fundo

90020-090

Irmandade Da Santa Casa de Misericordia de Porto Alegre, Porto Alegre

15090-000

Fundacao Faculdade Regional de Medicina de Sao Jose Do Rio Preto Hospital de Base - PPDS, São José do Rio Preto

05403-000

Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo, São Paulo

06000

CHU de Nice, Nice

060-8648

Hokkaido University Hospital, Hokkaido

650-0017

Kobe University Hospital, Hyōgo

232-0024

Yokohama City University Medical Center, Kanagawa

252-0375

Kitasato University Hospital, Kanagawa

321-0293

Dokkyo Medical University Hospital, Mibu-Machi

520-2192

Shiga University Of Medical Science Hospital, Shiga

157-8535

National Center for Child Health and Development, Tokyo

15-274

Uniwersytecki Szpital Kliniczny w Bialymstoku, Bia?ystok

85-048

In-VIVO Osrodek Badan Klinicznych, Bydgoszcz

Unknown

Uniwersyteckie Centrum Kliniczne, Gdansk

02-091

Dzieciecy Szpital Kliniczny UCK WUM, Warsaw

08950

Hospital Sant Joan de Deu - PIN, Barcelona

All Listed Sponsors
lead

Hoffmann-La Roche

INDUSTRY