LGMD R1 Natural History Study

RecruitingOBSERVATIONAL
Enrollment

100

Participants

Timeline

Start Date

January 31, 2024

Primary Completion Date

May 31, 2028

Study Completion Date

August 31, 2028

Conditions
Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2ALimb Girdle Muscular DystrophyLimb Girdle Muscular Dystrophy Type R1LGMD2A
Trial Locations (12)

23298

RECRUITING

Virginia Commonwealth University, Richmond

32610

NOT_YET_RECRUITING

University of Florida, Gainesville

43205

RECRUITING

Nationwide Children's Hospital, Columbus

46565

RECRUITING

The Community Health Clinic, Inc., Shipshewana

52242

RECRUITING

University of Iowa Hospitals and Clinics, Iowa City

55455

RECRUITING

University of Minnesota, Department of Neurology, Minneapolis

63110

RECRUITING

Washington University School of Medicine, St Louis

66160

RECRUITING

University of Kansas Medical Center, Kansas City

80045

RECRUITING

University of Colorado Anschutz Medical Campus, Aurora

92868

RECRUITING

University of California, Irvine, Orange

Unknown

NOT_YET_RECRUITING

Leiden University Medical Center, Leiden

NOT_YET_RECRUITING

Newcastle University, Newcastle upon Tyne

All Listed Sponsors
collaborator

Nationwide Children's Hospital

OTHER

collaborator

Washington University School of Medicine

OTHER

collaborator

University of Iowa

OTHER

collaborator

University of Florida

OTHER

collaborator

University of Minnesota

OTHER

collaborator

Newcastle University

OTHER

collaborator

University of Kansas Medical Center

OTHER

collaborator

University of Colorado, Denver

OTHER

collaborator

Indiana CHC (Community Health Clinic)

UNKNOWN

collaborator

University of California, Irvine

OTHER

lead

Virginia Commonwealth University

OTHER