ONC201 in H3 K27M-mutant Diffuse Glioma Following Radiotherapy (the ACTION Study)

PHASE3RecruitingINTERVENTIONAL
Enrollment

450

Participants

Timeline

Start Date

January 23, 2023

Primary Completion Date

August 31, 2026

Study Completion Date

August 31, 2026

Conditions
H3 K27MGlioma
Interventions
DRUG

Dordaviprone (ONC201)

Participants ≥ 52.5 kg will receive 625 mg of ONC201 (5 × 125-mg capsules) dosing days; participants \< 52.5 kg will receive a dose (and corresponding number of capsules) scaled by body weight and rounded to 125-mg increments.

DRUG

Dordaviprone (ONC201) + Placebo

Participants ≥ 52.5 kg will receive 625 mg of ONC201 (5 × 125-mg capsules) or matching placebo on dosing days; participants \< 52.5 kg will receive a dose (and corresponding number of capsules) scaled by body weight and rounded to 125-mg increments

OTHER

Placebo

Participants will receive placebo (same number of capsules as the ONC201 dose) on dosing days

Trial Locations (162)

1011

RECRUITING

Centre Hospitalier Universitaire Vaudois, Lausanne

2031

RECRUITING

Sydney Children's Hospital, Randwick

2065

RECRUITING

Royal North Shore Hospital, Sydney

2100

RECRUITING

Copenhagen University Hospital, Copenhagen

3084

RECRUITING

Olivia Newton-John Cancer Research Institute (ONJCRI), Heidelberg

5000

RECRUITING

F345 H.C. Andersen's Children's Hospital, Odense

RECRUITING

Odense Universitetshospital, Odense

5505

RECRUITING

Asan Medical Center, Seoul

6009

RECRUITING

Perth Children's Hospital, Nedlands

6591

RECRUITING

The Catholic University of Korea, Seoul St. Mary's Hospital, Seoul

7000

RECRUITING

Royal Hobart Hospital, Hobart

8035

RECRUITING

Hospital Universitario Vall d'Hebron, Barcelona

8091

RECRUITING

Universitätsspital Zürich, Zurich

8950

RECRUITING

Hospital Sant Joan de Deu, Esplugues de Llobregat

9000

RECRUITING

Aalborg Universitetshospital, Aalborg

10029

ACTIVE_NOT_RECRUITING

Children's Hospital at Montefiore Medical Center, New York

ACTIVE_NOT_RECRUITING

Montefiore Medical Park, New York

10032

ACTIVE_NOT_RECRUITING

Columbia University Medical Center, New York

10075

ACTIVE_NOT_RECRUITING

Lenox Hill Hospital, New York

10126

RECRUITING

Azienda Ospedaliera Città della Salute e della Scienza di Torino, Turin

10408

RECRUITING

National Cancer Center, Ilsandong-Gu, Goyang-Si

12208

ACTIVE_NOT_RECRUITING

Albany Medical Center, Albany

12351

RECRUITING

Vivantes Klinikum Neukölln, Berlin

13496

RECRUITING

CHA Bundang Medical Center, Bundang-Gu, Seongnam-Si

13620

RECRUITING

Seoul National University Bundang Hospital, Bundang-gu, Seongnam-si

RECRUITING

Seoul National University Hospital, Bundang-gu, Seongnam-si

14642

ACTIVE_NOT_RECRUITING

University of Rochester Medical Center, Rochester

15232

ACTIVE_NOT_RECRUITING

UPMC Children's Hospital of Pittsburgh, Pittsburgh

ACTIVE_NOT_RECRUITING

UPMC Hillman Cancer Center, Pittsburgh

19104

ACTIVE_NOT_RECRUITING

University of Pennsylvania, Philadelphia

19107

ACTIVE_NOT_RECRUITING

Thomas Jefferson University, Philadelphia

20007

ACTIVE_NOT_RECRUITING

MedStar Georgetown University Hospital, Washington D.C.

20089

RECRUITING

Istituto Clinico Humanitas, Rozzano

20132

RECRUITING

Ospedale San Raffaele S.r.l., Milan

20133

RECRUITING

Fondazione IRCCS Di Rilievo Nazionale Istituto Nazionale Neurologico Carlo Besta, Milan

21201

ACTIVE_NOT_RECRUITING

University of Maryland School of Medicine, Baltimore

22031

ACTIVE_NOT_RECRUITING

Inova Schar Cancer Institute, Fairfax

23507

ACTIVE_NOT_RECRUITING

Children's Hospital of The King's Daughter, Norfolk

27710

ACTIVE_NOT_RECRUITING

Duke Cancer Institute, Durham

28009

RECRUITING

Hospital Infantil Universitario Niño Jesus, Madrid

28041

RECRUITING

Hospital Universitario 12 de Octubre, Madrid

28050

RECRUITING

Hospital Universitario HM Sanchinarro, Madrid

28204

ACTIVE_NOT_RECRUITING

Levine Cancer Institute/ Atrium Health, Charlotte

30342

ACTIVE_NOT_RECRUITING

Children's Healthcare of Atlanta, Atlanta

31008

RECRUITING

Clinica Universidad Navarra, Pamplona

31096

RECRUITING

Rambam Medical Center, Haifa

32224

ACTIVE_NOT_RECRUITING

Mayo Clinic Jacksonville, Jacksonville

33176

ACTIVE_NOT_RECRUITING

Miami Cancer Institute, Miami

33331

WITHDRAWN

Cleveland Clinic Florida, Weston

33607

ACTIVE_NOT_RECRUITING

St Joseph's Children's Hospital of Tampa, Tampa

33612

ACTIVE_NOT_RECRUITING

Moffitt Cancer Center, Tampa

35128

RECRUITING

Istituto Oncologico Veneto, Padua

37007

RECRUITING

Complejo Asistencial Universitario de Salamanca - H. Clinico, Salamanca

40139

RECRUITING

Ospedale Bellaria, Bologna

40241

ACTIVE_NOT_RECRUITING

Norton Healthcare, Louisville

43210

ACTIVE_NOT_RECRUITING

Ohio State University, Columbus

44195

ACTIVE_NOT_RECRUITING

Cleveland Clinic, Cleveland

45147

RECRUITING

Universitätsklinikum Essen, Essen

45229

ACTIVE_NOT_RECRUITING

Cincinnati Children's Hospital Medical Center, Cincinnati

46026

RECRUITING

Hospital Universitari i Politecnic La Fe de Valencia - Adults, Valencia

RECRUITING

Hospital Universitari i Politecnic La Fe de Valencia - Pediatrics, Valencia

46202

ACTIVE_NOT_RECRUITING

Indiana University School of Medicine - Indianapolis, Indianapolis

48109

ACTIVE_NOT_RECRUITING

University of Michigan Hospital, Ann Arbor

49372

RECRUITING

Rabin Medical Center, Petah Tikva

50937

RECRUITING

Uniklinik Köln, Cologne

RECRUITING

Soroka University Medical Centre, Beersheba

52242

ACTIVE_NOT_RECRUITING

University of Iowa Hospitals & Clinics, Iowa City

53127

RECRUITING

Universitätsklinikum Bonn, Bonn

53792

ACTIVE_NOT_RECRUITING

University Of Wisconsin - Madison, Madison

55455

ACTIVE_NOT_RECRUITING

University of Minnesota, Minneapolis

55905

ACTIVE_NOT_RECRUITING

Mayo Clinic - Cancer Center - Rochester, Rochester

59405

WITHDRAWN

Benefis Hospital Sletten Cancer Institute, Great Falls

60528

RECRUITING

Klinikum der Johann-Wolfgang Goethe-Universitat, Frankfurt am Main

60611

ACTIVE_NOT_RECRUITING

Feinberg School of Medicine Northwestern University, Chicago

63110

ACTIVE_NOT_RECRUITING

Washington University School of Medicine/St. Louis Children's Hospital, St Louis

64239

RECRUITING

Tel Aviv Sourasky Medical Center, Tel Aviv

68114

ACTIVE_NOT_RECRUITING

University of Nebraska Medical Center, Omaha

68167

RECRUITING

Klinikum Mannheim Universitätsklinikum gGmbH, Manheim

69120

RECRUITING

University Clinic Heidelberg, Heidelberg

RECRUITING

Universitätsklinikum Heidelberg, Heidelberg

70121

ACTIVE_NOT_RECRUITING

Ochsner Medical Center - New Orleans, New Orleans

72076

RECRUITING

Universitätsklinikum Tübingen, Tübingen

73104

ACTIVE_NOT_RECRUITING

University of Oklahoma Peggy and Charles Stephenson Cancer Center, Oklahoma City

75246

ACTIVE_NOT_RECRUITING

Neuro-Oncology Associates, Dallas

75390

ACTIVE_NOT_RECRUITING

University of Texas Southwestern Medical Center, Dallas

77030

ACTIVE_NOT_RECRUITING

University of Texas MD Anderson Cancer Center, Houston

ACTIVE_NOT_RECRUITING

UT Health Houston Neurosciences - Texas Medical Center, Houston

78229

ACTIVE_NOT_RECRUITING

University of Texas - San Antonio - Health Science Center, San Antonio

78723

ACTIVE_NOT_RECRUITING

Dell Children's Medical Center of Central Texas, Austin

84112

ACTIVE_NOT_RECRUITING

University of Utah - Huntsman Cancer Institute, Salt Lake City

85006

ACTIVE_NOT_RECRUITING

Banner MD Anderson Cancer Center, Phoenix

85013

ACTIVE_NOT_RECRUITING

Barrow Neurological Institute, Phoenix

85016

ACTIVE_NOT_RECRUITING

Phoenix Childrens Hospital, Phoenix

85054

ACTIVE_NOT_RECRUITING

Mayo Clinic Arizona, Phoenix

86156

RECRUITING

Universitätsklinikum Augsburg, Augsburg

90027

ACTIVE_NOT_RECRUITING

Kaiser Permanente Los Angeles Medical Center, Los Angeles

90095

ACTIVE_NOT_RECRUITING

UCLA University of California Los Angeles, Los Angeles

90404

ACTIVE_NOT_RECRUITING

Providence Saint John's Cancer Institute, Santa Monica

91120

RECRUITING

Hadassah Ein Kerem Medical Center, Jerusalem

92093

ACTIVE_NOT_RECRUITING

UC San Diego Moores Cancer Center, La Jolla

92868

WITHDRAWN

Children's Hospital of Orange County, Orange

ACTIVE_NOT_RECRUITING

University of California Irvine, Orange

93053

RECRUITING

University Clinic Regensburg, Regensburg

94143

ACTIVE_NOT_RECRUITING

UCSF Benioff Children's Hospital, San Francisco

ACTIVE_NOT_RECRUITING

University of California San Francisco, San Francisco

94350

ACTIVE_NOT_RECRUITING

Stanford Cancer Center, Stanford

96826

ACTIVE_NOT_RECRUITING

Kapi'olani Medical Center for Women and Children, Honolulu

97239

ACTIVE_NOT_RECRUITING

Providence Health and Services St. Vincent Medical Center, Portland

98195

ACTIVE_NOT_RECRUITING

University of Washington, Seattle

229899

RECRUITING

KK Women's and Children's Hospital, Singapore

308433

RECRUITING

National Cancer Centre, Singapore

RECRUITING

National Neuroscience Institute, Singapore

999077

RECRUITING

Queen Mary Hospital, Hong Kong

4920235

RECRUITING

Schneider Children's Medical Center of Israel, Petah Tikvah

5262100

RECRUITING

Sheba Medical Center, Ramat Gan

06511

ACTIVE_NOT_RECRUITING

Yale University, New Haven

02114

ACTIVE_NOT_RECRUITING

Massachusetts General Hospital Cancer Center, Boston

02215

ACTIVE_NOT_RECRUITING

Dana Farber Cancer Institute, Boston

07753

ACTIVE_NOT_RECRUITING

Jersey Shore University Medical Center, Neptune City

07901

ACTIVE_NOT_RECRUITING

Overlook Medical Center, Summit

10032-3726

ACTIVE_NOT_RECRUITING

Laura & Isaac Perlmutter Cancer Center - NYU ACC, New York

C1426ABP

RECRUITING

FLENI Neurologia, Buenos Aires

Unknown

RECRUITING

Royal Brisbane and Women's Hospital, Herston

RECRUITING

Medical University of Vienna - Pediatrics, Vienna

RECRUITING

Hcor Research Institute, São Paulo

RECRUITING

Instituto Do Cancer Do Estado De São Paulo, São Paulo

RECRUITING

The University of Tokyo Hospital, Tokyo

01090

RECRUITING

Medical University of Vienna - Adults, Vienna

04023-062

RECRUITING

Hospital do GRAACC, São Paulo

T2N 2T9

RECRUITING

Tom Baker Cancer Cetre, Calgary

V5Z 4E6

RECRUITING

BC Cancer - The Vancouver Center, Vancouver

V6H 0B3

RECRUITING

Children's & Women's Health Care of BC, Vancouver

N6A 5W9

RECRUITING

London Health Sciences Centre, London

K1H 8L1

RECRUITING

Childrens Hospital of Eastern Ontario, Ottawa

M4N 3M5

RECRUITING

Sunnybrook Health Sciences Centre, Toronto

M5G 1X8

RECRUITING

Princess Margaret Hospital, Toronto

H2X 3E4

RECRUITING

Hopital Notre Dame, Lachapelle, Montreal

00144

WITHDRAWN

Istituto Nazionale Tumori Regina Elena, Rome

104-0045

RECRUITING

National Cancer Center Hospital, Chūō

812-8582

RECRUITING

National Hospital Organization Kyushu Cancer Center, Fukuoka

606-8507

RECRUITING

Kyoto University Hospital, Kyoto

534-0021

RECRUITING

Osaka City General Hospital, Osaka

060-8648

RECRUITING

Hokkaido University Hospital, Sapporo

3015 GD

RECRUITING

Erasmus MC, Rotterdam

3584 CX

RECRUITING

Universitair Medisch Centrum Utrecht Cancer Center, Utrecht

06273

RECRUITING

Gangnam Severance Hospital, Yonsei University Health System, Gangnam

06351

RECRUITING

Samsung Medical Center, Gangnam-Gu

03080

RECRUITING

Seoul National University Hospital, Jongno-Gu

03722

RECRUITING

Severance Hospital Yonsei University Health System, Seoul

08036

RECRUITING

Hospital Clinic de Barcelona, Barcelona

CB2 0QQ

RECRUITING

Addenbrooke's Hospital, Cambridge

G12 0YN

RECRUITING

Beatson West of Scotland Cancer Centre, Glasgow

G51 4TF

RECRUITING

Royal Hospital for Children (Glasgow), Glasgow

L7 8YA

RECRUITING

Clatterbridge Cancer Centre - Liverpool, Liverpool

M20 4BX

RECRUITING

The Christie NHS Foundation Trust, Manchester

SM2 5PT

RECRUITING

The Royal Marsden in Sutton, Surrey, Sutton

NE1 4LP

RECRUITING

Royal Victoria Infirmary, Newcastle upon Tyne

NE7 7DN

RECRUITING

Freeman Hospital, Newcastle upon Tyne

LS9 7TF

RECRUITING

St James University Hospital, Leeds

LS1 3EX

RECRUITING

The Leeds Teaching Hospitals NHS Trust, Leeds General Infimary, Leeds

SE19RT

RECRUITING

Guy's Hospital, London

Ox3 7LE

RECRUITING

Churchill Hospital, Oxford

Sponsors
All Listed Sponsors
lead

Jazz Pharmaceuticals

INDUSTRY