Neuromuscular Characterisation in Late Adolescent and Adult Cystinosis Patients

UnknownOBSERVATIONAL
Enrollment

20

Participants

Timeline

Start Date

September 22, 2022

Primary Completion Date

March 31, 2025

Study Completion Date

March 31, 2025

Conditions
Cystinosis
Trial Locations (2)

92380

NOT_YET_RECRUITING

Neurology Department, Raymond-Poincaré hospital, APHP, Garches

Unknown

RECRUITING

Department of Nephrology and Transplantation Centre de référence des Maladies Rénales Héréditaires de l'Enfant et de l'Adulte, Necker-Enfants Malades University Hospital, APHP, Paris

Sponsors
All Listed Sponsors
collaborator

Cystinosis Research Foundation

OTHER

lead

Assistance Publique - Hôpitaux de Paris

OTHER