Newborn Screening for Spinal Muscular Atrophy

RecruitingOBSERVATIONAL
Enrollment

45,000

Participants

Timeline

Start Date

March 8, 2022

Primary Completion Date

March 7, 2025

Study Completion Date

March 7, 2025

Conditions
Muscular Atrophy, Spinal
Trial Locations (8)

Unknown

RECRUITING

Buckinghamshire HealthCare Trust, Buckingham

RECRUITING

Milton Keynes University Hospital NHS Foundation Trust, Milton Keynes

RECRUITING

University of Oxford UK, Oxford

RECRUITING

St Mary's Maternity Hospital, Poole

RECRUITING

Queen Alexandra Hospital, Portsmouth

RECRUITING

Royal Berkshire NHS Foundation Trust, Reading

RECRUITING

Salisbury District Hospital, Salisbury

RECRUITING

Princess Anne Hospital, Southampton

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Novartis Gene Therapies

INDUSTRY

collaborator

Hoffmann-La Roche

INDUSTRY

collaborator

Oxford University Hospitals NHS Trust

OTHER

lead

University of Oxford

OTHER

NCT05481164 - Newborn Screening for Spinal Muscular Atrophy | Biotech Hunter | Biotech Hunter