1
Participants
Start Date
June 24, 2022
Primary Completion Date
December 8, 2022
Study Completion Date
February 2, 2023
MGTA-145
MGTA-145 will be administered as an IV infusion
Plerixafor
240 µg/kg administered subcutaneously
National Institutes of Health, Bethesda
St. Jude Children's Research Hospital, Memphis
Boston Children's Hospital, Boston
Lead Sponsor
Collaborators (1)
Genetix Biotherapeutics Inc.
INDUSTRY
Ensoma
INDUSTRY