Evaluation of VX-121/Tezacaftor/Deutivacaftor in Cystic Fibrosis (CF) Participants 1 Through 11 Years of Age

PHASE3RecruitingINTERVENTIONAL
Enrollment

210

Participants

Timeline

Start Date

June 21, 2022

Primary Completion Date

June 30, 2030

Study Completion Date

June 30, 2030

Conditions
Cystic Fibrosis
Interventions
DRUG

VX-121/TEZ/D-IVA

Fixed-dose combination for oral administration.

Trial Locations (38)

11042

COMPLETED

Cohen Children's Medical Center, Lake Success

15224

RECRUITING

UPMC Children's Hospital of Pittsburgh, Pittsburgh

30322

RECRUITING

The Emory Clinic / Children's Healthcare of Atlanta at Egleston, Atlanta

43205

RECRUITING

Nationwide Children's Hospital, Columbus

44106

RECRUITING

Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center, Cleveland

45229

RECRUITING

Cincinnati Children's Hospital Medical Center, Cincinnati

46202

RECRUITING

Riley Hospital for Children at Indiana University Health, Indianapolis

53792

ACTIVE_NOT_RECRUITING

American Family Childrens Hospital, Madison

55404

RECRUITING

Children's Respiratory and Critical Care Specialists, P.A., Children's Hospitals and Clinics of Minnesota, Minneapolis

60611

RECRUITING

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

63110

RECRUITING

Washington University School of Medicine / St. Louis Children's Hospital, St Louis

64108

RECRUITING

The Children's Mercy Hospital, Kansas City

77030

RECRUITING

Texas Children's Hospital - Wallace Tower, Houston

80045

RECRUITING

Children's Hospital of Colorado, Aurora

92868

RECRUITING

Children's Hospital of Orange County, Orange

94304

RECRUITING

Stanford University Clinical and Translational Research Unit, Palo Alto

97239

COMPLETED

Oregon Health & Science University, Portland

02115

RECRUITING

Boston Children's Hospital, Boston

05446

RECRUITING

Vermont Lung Center, Colchester

Unknown

RECRUITING

The Kids Research Institute Australia, Nedlands

RECRUITING

Women's and Children's Hospital, North Adelaide

RECRUITING

The Royal Children's Hospital, Parkville

RECRUITING

Queensland Children's Hospital, South Brisbane

RECRUITING

The Hospital for Sick Children, Toronto

RECRUITING

British Columbia Children's Hospital, Vancouver

RECRUITING

CHU Lyon - Hopital Femme Mere-Enfant, Bron

RECRUITING

Hopital Necker, Enfants Malades, Paris

RECRUITING

Charité Universitätsmedizin BerlinX, Berlin

RECRUITING

Kinderklinik III, Abt. fur Pneumologie, Essen

RECRUITING

Medizinische Hochschule Hannover, Hanover

RECRUITING

Erasmus Medical Center / Sophia Children's Hospital, Rotterdam

RECRUITING

Starship Children's Hospital, Grafton

COMPLETED

Sahlgrenska Universitetssjukhuset, Gothenburg

RECRUITING

Karolinska Universitetssjukhuset, Huddinge, Stockholm

COMPLETED

Inselspital - Universitaetsspital Bern, Bern

RECRUITING

Kinderspital Zurich, Zurich

RECRUITING

Children and Young Adults Research Unit, Cardiff

RECRUITING

Great Ormond Street Hospital for Children, London

All Listed Sponsors
lead

Vertex Pharmaceuticals Incorporated

INDUSTRY