A Study to Assess the Long-Term Safety and Efficacy of Donidalorsen in the Prophylactic Treatment of Hereditary Angioedema (HAE)

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

154

Participants

Timeline

Start Date

July 13, 2022

Primary Completion Date

December 31, 2026

Study Completion Date

March 31, 2027

Conditions
Hereditary Angioedema
Interventions
DRUG

Donidalorsen

Donidalorsen will be administered by SC injection.

Trial Locations (50)

1105

Ionis Investigative Site, Amsterdam

1431

Ionis Investigative Site, Sofia

1680

Ionis Investigative Site, Sofia

2650

Ionis Investigative Site, Edegem

12203

Ionis Investigative Site, Berlin

13385

Ionis Investigative Site, Marseille

17033

Ionis Investigative Site, Hershey

20097

Ionis Investigative Site, San Donato Milanese

28046

Ionis Investigative Site, Madrid

28117

Ionis Investigative Site, Mooresville

33613

Ionis Investigative Site, Tampa

34093

Ionis Investigative Site, Istanbul

35100

Ionis Investigative Site, Bornova

35128

Ionis Investigative Site, Padua

38700

Ionis Investigative Site, La Tronche

41013

Ionis Investigative Site, Seville

43235

Ionis Investigative Site, Columbus

45236

Ionis Investigative Site, Cincinnati

46026

Ionis Investigative Site, Valencia

48109

Ionis Investigative Site, Ann Arbor

48202

Ionis Investigative Site, Detroit

60590

Ionis Investigative Site, Frankfurt

63141

Ionis Investigative Site, St Louis

66103

Ionis Investigative Site, Kansas City

75012

Ionis Investigative Site, Paris

75231

Ionis Investigative Site, Dallas

80131

Ionis Investigative Site, Napoli

81675

Ionis Investigative Site, München

84107

Ionis Investigative Site, Murray

85253

Ionis Investigative Site, Paradise Valley

90146

Ionis Investigative Site, Palermo

90404

Ionis Investigative Site, Santa Monica

92037

Ionis Investigative Site, La Jolla

94598

Ionis Investigative Site, Walnut Creek

95123

Ionis Investigative Site, Catania

3104802

Ionis Investigative Site, Haifa

6423906

Ionis Investigative Site, Tel Aviv

7830604

Ionis Investigative Site, Ashkelon

02114

Ionis Investigative Site, Boston

K1H 1E4

Ionis Investigative Site, Ottawa

AB T6G 1Z1

Ionis Investigative Site, Edmonton

9713 AP

Ionis Investigative Site, Groningen

31-501

Ionis Investigative Site, Krakow

PR 00927

Ionis Investigative Site, San Juan

08035

Ionis Investigative Site, Barcelona

08907

Ionis Investigative Site, Barcelona

06230

Ionis Investigative Site, Altındağ

B9 5SS

Ionis Investigative Site, Birmingham

BS10 5NB

Ionis Investigative Site, Bristol

E1 2ES

Ionis Investigative Site, London

Sponsors
All Listed Sponsors
lead

Ionis Pharmaceuticals, Inc.

INDUSTRY