Study of AAV5-hFIX in Severe or Moderately Severe Haemophilia B

Active, not recruitingOBSERVATIONAL
Enrollment

9

Participants

Timeline

Start Date

March 18, 2021

Primary Completion Date

May 31, 2026

Study Completion Date

May 31, 2026

Conditions
Hemophilia B
Interventions
GENETIC

AAV5-hFIX

AAV5 containing a codon-optimized human factor IX gene

Trial Locations (6)

Unknown

Vivantes Klinikum im Friedrichshain, Berlin

Universitaetsklinikum Frankfurt - Klinikum der Johann Wolfgang Goethe Universitaet, Frankfurt

Amsterdam UMC - Locatie AMC, Amsterdam

Groningen UMC, Groningen

Erasmus MC, Rotterdam

Universitair Medisch Centrum Utrecht, Utrecht

Sponsors

Lead Sponsor

All Listed Sponsors
lead

CSL Behring

INDUSTRY