269
Participants
Start Date
July 6, 2022
Primary Completion Date
September 25, 2024
Study Completion Date
January 31, 2026
taldefgrobep alfa
DB Phase: 35 mg/50 mg weekly subcutaneous injection
Placebo
DB Phase: matching placebo 35 mg/50 mg weekly subcutaneous injection
taldefgrobep alfa
Extension Phase: 35 mg/50 mg weekly subcutaneous injection
Columbia University Medical Center, New York
Stony Brook University Hospital, Stony Brook
UPMC Children's Hospital of Pittsburgh, Pittsburgh
Penn State College of Medicine, Hershey
CHOP Children's Hospital of Philadelphia, Philadelphia
Donostia University Hospital, Donostia / San Sebastian
University of Virginia Children's Hospital, Charlottesville
Children's Hospital of The King's Daughters, Norfolk
Nemo-Brescia Clinical Center For Neuromuscular Diseases, Gussago
IRCCS NEUROLOGICAL INSTITUTE C. MONDINO CHILD and NEUROPSYCHIATRIC UNIT, Pavia
Duke University Medicine, Durham
Maternal-Child'S Hospital of Málaga, Regional University Hospital - Pediatric Neurology Unit, Málaga
Rare Disease Research, Atlanta
UF Health, Shands Hospital, Gainesville
Vanderbilt University Medical Center, Nashville
Irccs Institute of Neurological Sciences of Bologna - Bellaria Hospital, Bologna
Nationwide Children's Hospital, Columbus
University Hospital Essen (Public-Law Institution) - Dept. of Pediatrics I, Essen
Cincinnati Children's Hospital Medical Center, Cincinnati
La Fe University and Polytechnic Hospital, Valencia
Indiana University -Riley Research, Indianapolis
BSHS Office of Research, Grand Rapids
University of Iowa, Iowa City
Medical College of Wisconsin, Milwaukee
Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University in St. Louis, St Louis
University of Kansas Medical Center, Fairway
Neurology Rare Disease Center, Denton
Cook Children's Hospital, Fort Worth
UT Pediatric Neurosciences/Dell Children's Medical Center, Austin
University Hospital Freiburg, Center For Children and Adolescent Medicine, Dept. of Neuropediatrics and Muscle Disorders, Freiburg im Breisgau
Children's Hospital Colorado, Aurora
Dr. Von Haunersches Children'S Hospital - Lmu Munich, Munich
Phoenix Children's, Phoenix
Children's Hospital of Los Angeles, Los Angeles
UCSD & Rady Children's, La Jolla
UCSF Benioff Children's Hospital, Medical Center, San Francisco
MultiCare Institute of Research and Innovation, Tacoma
Boston Children's Hospital - Harvard, Boston
University Hospital Antwerp, Edegem
University Hospital Ghent, Ghent
University Hospital Leuven, Leuven
University Hospital Brno - Dept. of Pediatric Neurology, Brno
Motol University Hospital, Prague
Bambino Gesù Children'S Research Hospital Irccs - San Paolo Office Dept. of Neuroscience, Roma
University Medical Center Utrecht, Utrecht
University Clinical Centre in Gdansk - Dept. of Developmental Neurology, Gdansk
Heliodor Swiecicki Clinical Hospital At Medical University - Child and Adolescents Neurology Clinic, Poznan
The Children'S Memorial Health Institute - Dept. of Neurology and Epileptology, Warsaw
T. Marciniak Lower Silesian Specialist Hospital, Pediatric Neurology Dept., Wroclaw
Hospital Sant Joan de Déu, Esplugues de Llobregat
Royal Hospital For Children, Glasgow
John Radcliffe Hospital, Oxford
Lead Sponsor
Biohaven Pharmaceuticals, Inc.
INDUSTRY