Early Detection of Neuropathy in ATTRv

Active, not recruitingOBSERVATIONAL
Enrollment

47

Participants

Timeline

Start Date

February 14, 2022

Primary Completion Date

November 1, 2025

Study Completion Date

February 14, 2029

Conditions
Hereditary Amyloidosis, Transthyretin-Related
Interventions
DIAGNOSTIC_TEST

neurofilament light chain

Blood test

DIAGNOSTIC_TEST

In-vivo Meissner Corpuscle imaging

Imaging

DIAGNOSTIC_TEST

Nerve conduction study

Nerve conduction study

Trial Locations (1)

19104

University of Pennsylvania, Philadelphia

All Listed Sponsors
collaborator

Ionis Pharmaceuticals, Inc.

INDUSTRY

collaborator

AstraZeneca

INDUSTRY

lead

University of Pennsylvania

OTHER