Health-related Quality of Life, Symptom Severity, and Pain Among Patients With PIK3CA-related Overgrowth Spectrum: A Mixed-methods Observational Study

CompletedOBSERVATIONAL
Enrollment

77

Participants

Timeline

Start Date

May 16, 2022

Primary Completion Date

June 28, 2024

Study Completion Date

June 28, 2024

Conditions
PIK3CA-related Overgrowth Spectrum
Interventions
OTHER

Alpelisib

There was no treatment allocation. Patients administered alpelisib by prescription that were involved in Novartis' alpelisib managed access program were enrolled

Trial Locations (1)

07936

Novartis Investigative Site, East Hanover

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY