NCT05265767View on ClinicalTrials.gov

Hematopoietic Stem Cell Transplantation Gene Therapy for Treatment of Severe Hemophilia A

PHASE1CompletedINTERVENTIONAL
Enrollment

6

Participants

Timeline

Start Date

April 1, 2022

Primary Completion Date

June 28, 2024

Study Completion Date

June 28, 2024

Conditions
Hemophilia A
Interventions
BIOLOGICAL

Auto CD34+PBSC transduced with a lentiviral vector encoding a novel coagulation factor VIII transgene

Auto CD34+PBSC transduced with a lentiviral vector encoding a novel coagulation factor VIII transgene administered by IV infusion following conditioning regimen.

Trial Locations (1)

632517

Christian Medical College Vellore Ranipet Campus, Vellore

All Listed Sponsors
collaborator

Dr. H. Trent Spencer, Professor, Emory University of Medicine, Atlanta Ga, 30322

UNKNOWN

lead

Christian Medical College, Vellore, India

OTHER