Defining Endpoints in Becker Muscular Dystrophy

Active, not recruitingOBSERVATIONAL
Enrollment

80

Participants

Timeline

Start Date

April 13, 2022

Primary Completion Date

May 31, 2026

Study Completion Date

May 31, 2026

Conditions
Becker Muscular DystrophyMuscular DystrophiesMuscular Dystrophy in ChildrenMuscular Dystrophy, Becker
Trial Locations (11)

21205

Kennedy Krieger Institute, Baltimore

23298

Virginia Commonwealth University, Richmond

43205

Nationwide Children's Hospital, Columbus

52242

University of Iowa, Iowa City

55455

University of Minnesota, Minneapolis

63110

Washington University School of Medicine, St Louis

66160

University of Kansas Medical Center, Kansas City

80045

University of Colorado Anschutz Medical Campus, Aurora

92868

University of California, Irvine, Orange

Unknown

University of Auckland, Auckland

NE1 4EP

John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne

Sponsors
All Listed Sponsors
collaborator

Edgewise Therapeutics, Inc.

INDUSTRY

lead

Virginia Commonwealth University

OTHER