Research for Individualized Therapeutics in Rare Genetic Disease

Enrolling by invitationOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

November 24, 2021

Primary Completion Date

November 30, 2026

Study Completion Date

November 30, 2026

Conditions
Rare Genetic DiseaseUndiagnosed Diseases
Interventions
OTHER

Individualized drug matching per genetic disease

Patient phenotype and samples will be evaluated for individualized therapeutic drug development

Trial Locations (3)

32224

Mayo Clinic Florida, Jacksonville

55905

Mayo Clinic Rochester, Minneota

85259

Mayo Clinic in Arizona, Scottsdale

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Mayo Clinic

OTHER

NCT05236595 - Research for Individualized Therapeutics in Rare Genetic Disease | Biotech Hunter | Biotech Hunter