DMCRN-02-001: Assessing Pediatric Endpoints in DM1

RecruitingOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

August 24, 2022

Primary Completion Date

October 31, 2026

Study Completion Date

December 31, 2026

Conditions
Congenital Myotonic DystrophyCDM
Trial Locations (5)

14642

RECRUITING

University of Rochester Medical Center, Rochester

20162

RECRUITING

Centro Clinico NeMO, Milan

23298

RECRUITING

Virginia Commonwealth University, Richmond

66205

RECRUITING

University of Kansas Medical Center, Fairway

90095

RECRUITING

University of California, Los Angeles, Los Angeles

All Listed Sponsors
lead

Virginia Commonwealth University

OTHER