30
Participants
Start Date
June 6, 2022
Primary Completion Date
December 13, 2024
Study Completion Date
January 31, 2030
Mitapivat
Tablets or granules
Mitapivat-matching placebo
Tablets or granules
Charite - UB - CVK - Medizinische Klinik, Berlin
Children's Hospital of Philadelphia, Philadelphia
Duke University Medical Center, Durham
Hospital Universitario Infantil Nino Jesus, Madrid
Children's Healthcare of Atlanta - Emory, Atlanta
Hôpital Pellegrin, Bordeaux
St Jude's Children's Research Hospital, Memphis
Children's Hospital of Michigan, Detroit
UChicago Medicine, Chicago
UT Southwestern Medical Center, Dallas
Texas Children's Hospital, Houston
Children's Hospital Colorado, Aurora
Stanford Medicine, Palo Alto
Universitatsklinikum Wurzburg, Würzburg
Boston Children's Hospital, Boston
Centre hospitalier Universitaire de Sainte-Justine, Montreal
Universitair Medisch Centrum Utrecht, Utrecht
Hospital Universitario Vall d'Hebron, Barcelona
CHUV University Hospital of Lausanne, Lausanne
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY