49
Participants
Start Date
June 8, 2022
Primary Completion Date
May 3, 2024
Study Completion Date
June 30, 2029
Mitapivat
Tablets or granules
Mitapivat-matching placebo
Tablets or granules
Rigshospitalet, Copenhagen
Aarhus University Hospital, Aarhus
Weill Cornell Medical College, New York
Charite - UB - CVK - Medizinische Klinik, Berlin
Children's Hospital of Philadelphia, Philadelphia
Hospital Clinico Universitario Virgen de la Arrixaca, Madrid
Children's Healthcare of Atlanta - Emory, Atlanta
İstanbul Üniversitesi Tıp Fakültesi [Istanbul University Faculty of Medicine] Çocuk Sağlığı Enstitüsü [Institute of Child Health], Istanbul
UT Southwestern Medical Center, Dallas
Texas Children's Hospital, Houston
Phoenix Children's Hospital, Phoenix
Cure 4 the Kids Foundation, A Division of Roseman University of Health Sciences, Las Vegas
Stanford Medicine, Palo Alto
Boston Children's Hospital, Boston
Comprehensive Hemophilia Care Clinic at CHEO (Children's Hospital Eastern Ontario), Ottawa
Fakultní Nemocnice Olomouc, Olomouc
Universitair Medisch Centrum Utrecht, Utrecht
Hospital Universitario Vall d'Hebron, Barcelona
CHUV University Hospital of Lausanne, Lausanne
Ege University Faculty of Medicine, Izmir
Hacettepe University, Ankara
King's College Hospital NHS, London
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY