OASIS-HAE: A Study to Evaluate the Safety and Efficacy of Donidalorsen (ISIS 721744 or IONIS-PKK-LRx) in Participants With Hereditary Angioedema (HAE)

PHASE3CompletedINTERVENTIONAL
Enrollment

91

Participants

Timeline

Start Date

December 3, 2021

Primary Completion Date

November 9, 2023

Study Completion Date

November 9, 2023

Conditions
Hereditary Angioedema
Interventions
DRUG

Donidalorsen

Donidalorsen was administered by SC injection.

DRUG

Placebo

Donidalorsen-matching placebo was administered by SC injection.

Trial Locations (51)

1020

Ionis Investigative Site, Brussels

1200

Ionis Investigative Site, Brussels

1431

Ionis Investigative Site, Sofia

1680

Ionis Investigative Site, Sofia

2650

Ionis Investigative Site, Edegem

5000

Ionis Investigative Site, Odense

6230

Ionis Investigative Site, Ankara

8907

Ionis Investigative Site, Barcelona

12203

Ionis Investigative Site, Berlin

13385

Ionis Investigative Site, Marseille

17033

Ionis Investigative Site, Hershey

20138

Ionis Investigative Site, Milan

28046

Ionis Investigative Site, Madrid

33613

Ionis Investigative Site, Tampa

34093

Ionis Investigative Site, Istanbul

35100

Ionis Investigative Site, Izmir

35128

Ionis Investigative Site, Padua

38700

Ionis Investigative Site, La Tronche

41013

Ionis Investigative Site, Seville

43235

Ionis Investigative Site, Columbus

43617

Ionis Investigative Site, Toledo

46026

Ionis Investigative Site, Valencia

48109

Ionis Investigative Site, Ann Arbor

60590

Ionis Investigative Site, Frankfurt

63110

Ionis Investigative Site, St Louis

66205

Ionis Investigative Site, Kansas City

75012

Ionis Investigative Site, Paris

75231

Ionis Investigative Site, Dallas

78278

Ionis Investigative Site, Ashkelon

80131

Ionis Investigative Site, Napoli

80907

Ionis Investigative Site, Colorado Springs

81675

Ionis Investigative Site, Munich

84107

Ionis Investigative Site, Murray

85251

Ionis Investigative Site, Scottsdale

90146

Ionis Investigative Site, Palermo

90404

Ionis Investigative Site, Santa Monica

92122

Ionis Investigative Site, San Diego

94598

Ionis Investigative Site, Walnut Creek

95124

Ionis Investigative Site, Catania

3104802

Ionis Investigative Site, Haifa

6423906

Ionis Investigative Site, Tel Aviv

02114

Ionis Investigative Site, Boston

K1G6C6

Ionis Investigative Site, Ottawa

T6G 2G3

Ionis Investigative Site, Edmonton

1105 AZ

Ionis Investigative Site, Amsterdam

9713 GZ

Ionis Investigative Site, Groningen

31-503

Ionis Investigative Site, Krakow

08035

Ionis Investigative Site, Barcelona

B9 5SS

Ionis Investigative Site, Birmingham

BS10 5NB

Ionis Investigative Site, Bristol

E1 1FR

Ionis Investigative Site, London

Sponsors
All Listed Sponsors
lead

Ionis Pharmaceuticals, Inc.

INDUSTRY