Natural History Study in Pediatric Patients With MYBPC3 Mutation-associated Cardiomyopathy

RecruitingOBSERVATIONAL
Enrollment

200

Participants

Timeline

Start Date

November 1, 2021

Primary Completion Date

June 30, 2028

Study Completion Date

June 30, 2028

Conditions
Cardiomyopathy
Trial Locations (29)

8950

RECRUITING

Hospital Sant Joan de Déu Barcelona, Barcelona

10029

RECRUITING

Mount Sinai, New York

10032

RECRUITING

Columbia University Irving Medical Center, New York

10467

RECRUITING

Montefiore Medical Center, Albert Einstein College of Medicine, The Bronx

11042

RECRUITING

Cohen Children's Medical Center, Lake Success

15224

RECRUITING

University of Pittsburgh Medical Center - Children's Hospital of Pittsburgh, Pittsburgh

17601

RECRUITING

Cardiology Care for Children, Lancaster

19104

RECRUITING

Children's Hospital of Philadelphia, Philadelphia

19803

RECRUITING

Nemours Alfred I. Dupont Hospital for Children, Wilmington

28003

RECRUITING

Hospital General Universitario Gregorio Marañón, Madrid

33021

RECRUITING

Joe DiMaggio Children's Hospital, Hollywood

36312

RECRUITING

Hospital Alvaro Cunqueiro - Clinico Universitario Vigo, Vigo

44062

RECRUITING

DDC Clinic Center for Special Needs Children, Middlefield

44195

RECRUITING

Cleveland Clinic Main Campus, Cleveland

45229

RECRUITING

Cincinnati Children's Hospital Medical Center, Cincinnati

63110

RECRUITING

St. Louis Children's Hospital, St Louis

64108

RECRUITING

Children's Mercy Hospital Kansas, Kansas City

72202

RECRUITING

Arkansas Children's Hospital, Little Rock

75207

RECRUITING

Children's Medical Center Dallas, Dallas

77030

RECRUITING

Texas Children's Hospital, Houston

80045

RECRUITING

University of Colorado Hospital - Anschutz Medical Campus, Aurora

90027

RECRUITING

Children's Hospital Los Angeles, Los Angeles

92123

RECRUITING

Rady Children's Hospital - San Diego, San Diego

95817

RECRUITING

University of California Davis Health, Sacramento

T6G 2B7

RECRUITING

University of Alberta Hospital, Edmonton

Unknown

RECRUITING

The Hospital for Sick Children, Toronto

G12 0XH

RECRUITING

NHS Greater Glasgow and Clyde, Glasgow

SW3 6NP

RECRUITING

Royal Brompton & Harefield NHS Foundation Trust, London

WC1N 3JH

RECRUITING

Great Ormond Street Hospital for Children NHS Foundation Trust, London

Sponsors
All Listed Sponsors
lead

Tenaya Therapeutics

INDUSTRY

NCT05112237 - Natural History Study in Pediatric Patients With MYBPC3 Mutation-associated Cardiomyopathy | Biotech Hunter | Biotech Hunter