31
Participants
Start Date
February 22, 2022
Primary Completion Date
September 16, 2025
Study Completion Date
September 16, 2025
Mayo Clinic Rochester, Rochester
UCSF Benioff Children's Hospital, Oakland
Hospital Pequeno Principe, Curitiba
Hospital de Clinicas de Porto Alegre, Porto Alegre
Hopital d'Enfants CHU Timone, Marseille
Armand-Trousseau Children's Hospital - CHU Paris Est, Paris
Hôpital des Enfants - CHU Toulouse Purpan, Toulouse
Universtitäsklinikum Giessen und Marburg, Giessen
LMU - Klinikum der Universitaet Muenchen - Neurologische Klinik und Poliklinik, Munich
Universita' di Catania, Catania
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan
University Hospital Friuli Centrale, Udine
Great Ormond Street Hospital NHSFT, London
Lead Sponsor
Azafaros A.G.
INDUSTRY