NCT05092685View on ClinicalTrials.gov

Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEn

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

November 1, 2023

Primary Completion Date

June 30, 2026

Study Completion Date

June 30, 2027

Conditions
Ornithine Transcarbamylase Deficiency
Interventions
GENETIC

AAVLK03hOTC

Peripheral intravenous infusion of AAVLK03hOTC.

Trial Locations (1)

WC1N 3JH

RECRUITING

Great Ormond Street Hospital, London

All Listed Sponsors
lead

University College, London

OTHER