127
Participants
Start Date
February 1, 2022
Primary Completion Date
November 12, 2024
Study Completion Date
April 29, 2025
OAV101
Gene therapy
Sham control
The sham procedure will consist of a small needle prick on the lower back at the location where the LP injection is normally made. The needle will break the skin, but no needle insertion for lumbar puncture will occur.
Red Cross War Memorial Childrens Hospital, Cape Town
Siriraj Hospital, Bangkok
Novartis Investigative Site, Riyadh
Clinic for Special Children, Strasburg
Children's Specialty Group/CHKD, Norfolk
St Jude Children's Research Hospital, Memphis
Hospital Civil De Guadalajara Fray Antonio Alcalde, Guadalajara
Novartis Investigative Site, Kuala Lumpur
Novartis Investigative Site, Kuala Lumpur
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Kaohsiung Medical University Hospital, Kaohsiung City
National Children's Hospital, Hanoi
Peking University First Hospital, Beijing
Novartis Investigative Site, Beijing
Novartis Investigative Site, Beijing
AIIMS, Ansari Nagar, New Delhi
Novartis Investigative Site, Singapore
Novartis Investigative Site, Hangzhou
Novartis Investigative Site, Chongqing
P.D. Hinduja National Hospital & MRC, Mumbai
Novartis Investigative Site, Hyderabad
Novartis Investigative Site, Guangzhou
Novartis Investigative Site, Shenzhen
Novartis Investigative Site, Chengdu
Novartis Investigative Site, Kolkata
Connecticut Children's Medical Center, Farmington
Novartis Investigative Site, Curitiba
Novartis Investigative Site, São Paulo
Paediatric Neurology, Copenhagen
Sir Ganga Ram Hospital, New Delhi
Novartis Investigative Site, Mexico City
Lead Sponsor
Novartis Pharmaceuticals
INDUSTRY