Higher Dose of Alglucosidase Alpha for Pompe Disease

Not yet recruitingOBSERVATIONAL
Enrollment

36

Participants

Timeline

Start Date

September 1, 2021

Primary Completion Date

December 31, 2023

Study Completion Date

December 31, 2026

Conditions
Glycogen Storage Disease Type II
Interventions
DRUG

Alglucosidase Alfa

Standard dose: 20-25 mg/kg every other week; Higher dose: \>25 mg/kg every other week.

All Listed Sponsors
lead

Taipei Veterans General Hospital, Taiwan

OTHER_GOV

NCT05017402 - Higher Dose of Alglucosidase Alpha for Pompe Disease | Biotech Hunter | Biotech Hunter