The Effect of Enzyme Replacement Therapy in Mucopolysaccharidosis

NACompletedINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

February 1, 2020

Primary Completion Date

March 20, 2021

Study Completion Date

March 27, 2021

Conditions
Mucopolysaccharidosis
Interventions
DRUG

Enzyme Replacement Agent

Enzyme replacement therapy is one such treatment and used for the management of some subtypes of MPS disease. Enzyme replacement therapy (ERT) is based on the concept of replacing the missing enzyme in the circulation to prevent the build-up of glycosaminoglycan (GAG) in the tissues

Trial Locations (1)

27144

Serkan Usgu, Gaziantep

All Listed Sponsors
lead

Hasan Kalyoncu University

OTHER

NCT05006222 - The Effect of Enzyme Replacement Therapy in Mucopolysaccharidosis | Biotech Hunter | Biotech Hunter