Extension Study to Evaluate Safety and Tolerability of Oral Dersimelagon (MT-7117) in Subjects With Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP)

PHASE3RecruitingINTERVENTIONAL
Enrollment

301

Participants

Timeline

Start Date

August 10, 2021

Primary Completion Date

December 31, 2027

Study Completion Date

December 31, 2027

Conditions
EPPXLP
Interventions
DRUG

MT-7117

MT-7117

Trial Locations (51)

1000

NOT_YET_RECRUITING

University Multi-Profile Hospital for Active Treatment (UMHAT) St. Ivan Rilski, Sophia

2050

NOT_YET_RECRUITING

Royal Prince Alfred Hospital, Camperdown

3050

RECRUITING

Royal Melbourne Hospital (RMH), Parkville

4066

RECRUITING

Wesley Medical Research, Brisbane

8036

RECRUITING

Hospital Clínic de Barcelona, Barcelona

10029

RECRUITING

Icahn School of Medicine at Mount Sinai (ISSMS)-The Mount Sinai Hospital (MSH), New York

10117

RECRUITING

Charite - Universitaetsmedizin Berlin, Berlin

12100

NOT_YET_RECRUITING

Azienda Sanitaria Ospedaliera Santa Croce E Carle - Cuneo, Cuneo CN

14186

RECRUITING

Karolinska University Hospital, Stockholm

16128

NOT_YET_RECRUITING

Ospedalle Galliera, Genova GE

19107

RECRUITING

Thomas Jefferson University, Philadelphia

19141

NOT_YET_RECRUITING

Einstein Medical Center, Philadelphia, Philadelphia

20122

RECRUITING

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico di Milano, Milan

25123

RECRUITING

Azienda Ospedaliera Spedali Civili di Brescia-Universita degli Studi Di Brescia, Brescia BS

27157

RECRUITING

Wake Forest University Baptist Health, Winston-Salem

28041

RECRUITING

Hospital Universitario, Madrid

33000

NOT_YET_RECRUITING

Centre Hospitalier Universitaire de Bordeaux - Hopital Saint - Andre, Bordeaux

33136

NOT_YET_RECRUITING

University Of Miami School Of Medicine, Center For Liver Diseases, Miami

34137

NOT_YET_RECRUITING

Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Materno-Infantile - Burlo Garofolo - Clinica Pediatrica, Trieste TS

41125

ACTIVE_NOT_RECRUITING

U.O.C. Medicina Interna Azienda ospedaliero Universitaria Policlinico di Modena, Modena

43215

RECRUITING

Remington-Davis Clinical Research, Columbus

44000

NOT_YET_RECRUITING

CHU Nantes, Nantes

44106

NOT_YET_RECRUITING

Cleveland Clinic - Taussig Cancer Institute, Cleveland

46014

NOT_YET_RECRUITING

Hospital General Universitario De Valencia, Valencia

48202

NOT_YET_RECRUITING

Henry Ford Health System, Detroit

64131

RECRUITING

Kansas City Research Institute, Kansas City

75018

NOT_YET_RECRUITING

Hospital Bichat-Hopitaux Universitaires Paris Nord Val de Seine, Paris

77555

RECRUITING

The University of Texas Medical Branch (UTMB), Galveston

92647

RECRUITING

Marvel Clinical Research, LLC, Huntington Beach

92700

NOT_YET_RECRUITING

Assistance Publique-Hopitaux de Paris (AP-HP) - Hopital Louis-Mourier, Colombes

94143

NOT_YET_RECRUITING

University of California at San Francisco - CSF Porphyria Center, San Francisco

98109

RECRUITING

University of Washington-Seattle Cancer Care Alliance, Seattle

5300144

RECRUITING

IFO-San Gallicano IRCCS, Rome

02114

NOT_YET_RECRUITING

Massachusetts General Hospital, Boston

02135-3211

RECRUITING

MetroBoston Clinical Partners, LLC, Brighton

Edmonton AB T6G 2G3

RECRUITING

University of Alberta Hospital, Edmonton

140 21

NOT_YET_RECRUITING

Institute for Clinical and Experimental Medicine - IKEM, Prague

650-0017

RECRUITING

Kobe University Hospital, Kobe

921-8035

COMPLETED

Sophia Dermatology Clinic, Kanazawa

569-8686

RECRUITING

Osaka Medical College Hospital, Takatsuki

108-0073

NOT_YET_RECRUITING

Tokyo Saiseikai Central Hospital, Minato-ku

930-0194

RECRUITING

Toyama University Hospital, Sugitani

730-8670

NOT_YET_RECRUITING

Mazda Hospital of Mazda Motor Corporation, Hiroshima

431-3125

NOT_YET_RECRUITING

Hamamatsu University Hospital, Shizuoka

3015 GD

NOT_YET_RECRUITING

Erasmus MC, Universitair Medisch Centrum Rotterdam, Rotterdam

N5021

RECRUITING

Haukeland University Hospital, Bergen

02-776

NOT_YET_RECRUITING

Instytut hematologii i Transfuzjologii, Warsaw

M6 8HD

RECRUITING

Salford Royal NHS Foundation Trust, Manchester

SE1 7EH

RECRUITING

St. John's Institute of Dermatology-Guy's & St Thomas' NHS Foundation Trust, London

SE1 9RT

ACTIVE_NOT_RECRUITING

Evelina London Children's Hospital - Guy's & St Thomas' NHS Foundation Trust, London

SO16 6YD

NOT_YET_RECRUITING

Southampton General Hospital - University Hospital Southampton NHS Foundation Trust, Southampton

All Listed Sponsors
lead

Mitsubishi Tanabe Pharma America Inc.

INDUSTRY