Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008

CompletedOBSERVATIONAL
Enrollment

13

Participants

Timeline

Start Date

July 2, 2021

Primary Completion Date

September 22, 2023

Study Completion Date

September 22, 2023

Conditions
Pyruvate Kinase Deficiency
Trial Locations (3)

20122

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milan

02114

Massachusetts General Hospital, Boston

3508 GA

Universitair Medisch Centrum Utrecht, Utrecht

Sponsors
All Listed Sponsors
lead

Agios Pharmaceuticals, Inc.

INDUSTRY