(HARBOR) Study to Evaluate Efficacy and Safety of BLU-263 Versus Placebo in Patients With Indolent Systemic Mastocytosis

PHASE2/PHASE3RecruitingINTERVENTIONAL
Enrollment

534

Participants

Timeline

Start Date

November 30, 2021

Primary Completion Date

September 30, 2032

Study Completion Date

September 30, 2032

Conditions
Indolent Systemic MastocytosisSmoldering Systemic Mastocytosis
Interventions
DRUG

Elenestinib

Elenestinib oral tablet

DRUG

Placebo

Placebo oral tablet

Trial Locations (53)

3004

RECRUITING

The Alfred Hospital, Melbourne

4021

RECRUITING

Kepler Universitatsklinikum, Med Campus III. Clinic of Internal Medicine 3 - Hematology and Oncology, Linz

6000

RECRUITING

Luzerner Kantonsspital, Lucerne

10032

RECRUITING

Columbia University Medical Center, New York

12203

RECRUITING

Charité - Universitätsmedizin Berlin Institute of Allergology, Berlin

14263

RECRUITING

Roswell Park Cancer Institute, Buffalo

20122

RECRUITING

UOC Ematologia, Milan

20246

RECRUITING

University Clinic Hamburg Eppendorf, Hamburg

27100

RECRUITING

S.C. Ematologia Fondazione I.R.C.C.S. Policlinico San Matteo, Pavia

28034

RECRUITING

Hospital Universitario Ramon y Cajal, Madrid

35294

RECRUITING

University of Alabama at Birmingham, Birmingham

37126

RECRUITING

Unità Operativa di Allergologia Azienda Ospedaliera Universitaria Integrata di Verona, Verona

38043

RECRUITING

CHU Grenoble, Grenoble

40138

RECRUITING

Unita Operativa di Ematologia AOU Policlinico S. Orsola-Malpighi, Bologna

44093

RECRUITING

CHU de Nantes, Nantes

45071

RECRUITING

Hospital Virgen del Valle - Instituto de Estudios de Mastocitosis de Castilla-La Mancha, Toledo

45219

RECRUITING

University of Cincinnati Medical Center, Cincinnati

47014

RECRUITING

Dipartimentod i Oncoematologia Istituto Scientifico Romagnolop er lo studio e la cura dei tumori (IRST)- IRCCS, Meldola

48109

RECRUITING

Michigan Medicine University of Michigan, Ann Arbor

50134

RECRUITING

SOD Ematologia (Ambulatori)- AOUC Azienda Ospedaliero Universitaria Careggi, Florence

55902

RECRUITING

Mayo Clinic, Rochester

68167

RECRUITING

Universitätsmedizin Mannheim III. Medizinische Klinik Universität Heidelberg Medizinische Fakultät Mannheim, Mannheim

75013

RECRUITING

Hôpital de la Pitié Salpétrière, Paris

75015

RECRUITING

Hôpital Necker - Départementd 'HématologieA dultes, Paris

77030

RECRUITING

The University of Texas, MD Anderson Cancer Center, Houston

80000

RECRUITING

CHU Amiens-Picardie, Amiens

80377

RECRUITING

LMU Klinikum, Munich

84112

RECRUITING

Huntsman Cancer Institute, University of Utah, Salt Lake City

84131

RECRUITING

S.S.D. Immunologia Clinica e Allergologia Azienda Ospedaliera Universitaria San Giovanni di Dio e Ruggi d'Aragona, Salerno

86000

RECRUITING

CHU de Poitiers, Poitiers

87042

RECRUITING

CHU de Limoges, Limoges

91054

RECRUITING

University Clinic Erlangen, Erlangen

94305

RECRUITING

Stanford Cancer Institute, Palo Alto

02115

RECRUITING

Brigham and Women's Hospital, Boston

Unknown

RECRUITING

Princess Alexandra Hospital, Woolloongabba

RECRUITING

Unitversitair Ziekenhuis Antwerpen, Edegem

RECRUITING

CHU de Caen, Caen

RECRUITING

CHU Toulouse - Hopital Larrey, Toulouse

RECRUITING

Universitätsklinikum RWTH Aachen Klinik für Hämatologie, Onkologie, Hämostaseologie und Stammzelltransplantation, Aachen

RECRUITING

Hospital Universitario Vall d'Hebron, Barcelona

3015 GD

RECRUITING

ErasmusMC, Rotterdam

9713 GZ

RECRUITING

University Medical Center Groningen, Groningen

N-0424

RECRUITING

Oslo University Hospital, Oslo

1169-050

RECRUITING

Centro Hospitalar de Lisboa Central, E.P.E. - Hospital de Santo Antonio dos Capuchos, Lisbon

4099-001

RECRUITING

CHUPorto, EPE - Hospital de Santo António, Porto

4200-139

RECRUITING

Centro Hospitalar Universitario Sao Joao, E.P.E., Porto

751 85

RECRUITING

Uppsala University Hospital, Uppsala

C-4031

RECRUITING

University Hospital Basel, Basel

CF14 4XW

RECRUITING

University Hospital of Wales, Cardiff

RECRUITING

University Hospital of Wales, Cardiff

SE1 7EH

RECRUITING

Guy's and St Thomas's NHS Foundation Trust, London

OX3 7LE

RECRUITING

Cancer and Haematology Centre, Oxford

PL6 8DH

RECRUITING

University Hospital Plymouth NHS Trust, Plymouth

All Listed Sponsors
lead

Blueprint Medicines Corporation

INDUSTRY

NCT04910685 - (HARBOR) Study to Evaluate Efficacy and Safety of BLU-263 Versus Placebo in Patients With Indolent Systemic Mastocytosis | Biotech Hunter | Biotech Hunter