Hepatic Histopathology in Urea Cycle Disorders

RecruitingOBSERVATIONAL
Enrollment

70

Participants

Timeline

Start Date

February 24, 2022

Primary Completion Date

June 30, 2026

Study Completion Date

June 30, 2026

Conditions
Urea Cycle DisorderOrnithine Transcarbamylase DeficiencyCitrullinemia 1ARGI DeficiencyASL DeficiencyArgininosuccinic AciduriaASS DeficiencyHyperargininemiaCarbamyl Phosphate Synthetase DeficiencyNAGS Deficiency
Trial Locations (2)

20010

NOT_YET_RECRUITING

Children's National Medical Center, Washington D.C.

77030

RECRUITING

Baylor College of Medicine, Houston

All Listed Sponsors
collaborator

Children's National Research Institute

OTHER

lead

Baylor College of Medicine

OTHER