Efficacy and Safety of Iptacopan (LNP023) in Adult Patients With Atypical Hemolytic Uremic Syndrome Naive to Complement Inhibitor Therapy

PHASE3RecruitingINTERVENTIONAL
Enrollment

50

Participants

Timeline

Start Date

January 17, 2022

Primary Completion Date

September 19, 2028

Study Completion Date

March 29, 2029

Conditions
Atypical Hemolytic Uremic Syndrome
Interventions
DRUG

Iptacopan

Iptacopan 200mg twice daily oral

Trial Locations (68)

1000

RECRUITING

Novartis Investigative Site, Ljubljana

1090

RECRUITING

Novartis Investigative Site, Vienna

6020

RECRUITING

Novartis Investigative Site, Innsbruck

10461

RECRUITING

Montefiore Medical Center ., The Bronx

12808

RECRUITING

Novartis Investigative Site, Prague

23298

RECRUITING

Virginia Commonwealth University, Richmond

27710

RECRUITING

Duke University Medical Center, Durham

33136

RECRUITING

University Of Miami, Miami

33305

RECRUITING

Novartis Investigative Site, Taoyuan District

35233

RECRUITING

Uni Of Alabama At Birmingham, Birmingham

40447

RECRUITING

Novartis Investigative Site, Taichung

43210

RECRUITING

Comprehensive Transplant Ctr at OSU, Columbus

44195

RECRUITING

Cleveland Clinic Foundation, Cleveland

55455

RECRUITING

University of Minnesota, Minneapolis

63110

RECRUITING

WA Uni School Of Med, St Louis

71110

RECRUITING

Novartis Investigative Site, Heraklion Crete

75390

RECRUITING

UT Southwestern Medical Center, Dallas

76502

RECRUITING

Baylor Scott and White Research, Temple

83305

RECRUITING

Novartis Investigative Site, Bratislava

90033

RECRUITING

USC Norris Cancer Center, Los Angeles

90095

RECRUITING

Univ of California at Los Angeles, Los Angeles

90502

RECRUITING

Harbor-UCLA Medical Center ., Torrance

92868

RECRUITING

Univ Cali Irvine ALS Neuromuscular, Orange

100034

RECRUITING

Novartis Investigative Site, Beijing

100191

RECRUITING

Novartis Investigative Site, Beijing

100730

RECRUITING

Novartis Investigative Site, Beijing

160012

RECRUITING

Novartis Investigative Site, Chandigarh

200025

RECRUITING

Novartis Investigative Site, Shanghai

210009

RECRUITING

Novartis Investigative Site, Nanjing

226014

RECRUITING

Novartis Investigative Site, Lucknow

264000

RECRUITING

Novartis Investigative Site, Yantai

411011

RECRUITING

Novartis Investigative Site, Pune

440015

RECRUITING

Novartis Investigative Site, Nagpur

500012

RECRUITING

Novartis Investigative Site, Hyderabad

510080

RECRUITING

Novartis Investigative Site, Guangzhou

600006

RECRUITING

Novartis Investigative Site, Chennai

695011

RECRUITING

Novartis Investigative Site, Thiruvananthapuram

710063

RECRUITING

Novartis Investigative Site, Shanxi

20007 2197

RECRUITING

Georgetown University Lombardi Cancer Center, Washington D.C.

02115

RECRUITING

Brigham and Womens Hospital, Boston

08901

RECRUITING

Rut Univ for Translational Med Scie, New Brunswick

87131-0001

RECRUITING

University of New Mexico, Albuquerque

45267-0585

RECRUITING

University of Cincinnati, Cincinnati

60430 370

RECRUITING

Novartis Investigative Site, Fortaleza

71635-580

RECRUITING

Novartis Investigative Site, Brasília

30150-221

RECRUITING

Novartis Investigative Site, Belo Horizonte

50740-900

RECRUITING

Novartis Investigative Site, Pernambuco

90035-074

RECRUITING

Novartis Investigative Site, Porto Alegre

18618-970

RECRUITING

Novartis Investigative Site, Botucatu

01327 001

RECRUITING

Novartis Investigative Site, São Paulo

04038-002

RECRUITING

Novartis Investigative Site, São Paulo

05403 000

RECRUITING

Novartis Investigative Site, São Paulo

22270-60

RECRUITING

Novartis Investigative Site, Rio de Janeiro

40301-155

RECRUITING

Novartis Investigative Site, Salvador

708 52

RECRUITING

Novartis Investigative Site, Ostrava

146 24

RECRUITING

Novartis Investigative Site, Prague

570 10

RECRUITING

Novartis Investigative Site, Thessaloniki

115 27

RECRUITING

Novartis Investigative Site, Athens

632 004

RECRUITING

Novartis Investigative Site, Vellore

350-0495

RECRUITING

Novartis Investigative Site, Iruma-gun

693 8501

RECRUITING

Novartis Investigative Site, Izumo

113 8655

RECRUITING

Novartis Investigative Site, Bunkyo Ku

03601

RECRUITING

Novartis Investigative Site, Martin

03080

RECRUITING

Novartis Investigative Site, Seoul

03722

RECRUITING

Novartis Investigative Site, Seoul

06591

RECRUITING

Novartis Investigative Site, Seoul

NW1 2BU

RECRUITING

Novartis Investigative Site, London

NE7 7DN

RECRUITING

Novartis Investigative Site, Newcastle upon Tyne

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY