Longitudinal Study of Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases.

RecruitingOBSERVATIONAL
Enrollment

100

Participants

Timeline

Start Date

March 1, 2021

Primary Completion Date

March 31, 2031

Study Completion Date

March 31, 2031

Conditions
Inherited DiseaseRare DiseasesMetabolic DiseaseUndiagnosed DiseaseNeurologic DisorderNeuro-Degenerative Disease
Interventions
OTHER

collection of data

collection of retrospective and prospective data from adult patients with ultra-rare inherited neurological diseases

Trial Locations (1)

20133

RECRUITING

Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan

All Listed Sponsors
lead

Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta

OTHER