45
Participants
Start Date
May 4, 2021
Primary Completion Date
August 31, 2025
Study Completion Date
August 31, 2025
EDIT-301
Administered by IV infusion after myeloablative conditioning with busulfan.
Columbia University Medical Center - Department of Pediatrics, New York
Columbia University Medical Center, New York
Children's Hospital of Philadelphia, Philadelphia
The University of North Carolina at Chapel Hill, Chapel Hill
Atrium Health, Charlotte
Medical University of South Carolina, Charleston
Children's Healthcare of Atlanta, Atlanta
Johns Hopkins All Children's Hospital, St. Petersburg
Tristar Medical Group Children's Specialists/Sarah Cannon Center for Blood Cancers, Nashville
University of Mississippi Medical Center, Jackson
Nationwide Children's Hospital, Columbus
The James Cancer Hospital, Columbus
University Hospitals Rainbow Babies & Children's Hospital, Cleveland
Cleveland Clinic, Cleveland
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Texas Oncology - Baylor Charles A. Sammons Cancer Center, Dallas
Cook Children's, Fort Worth
Children's Hospital Colorado, Aurora
UCSF Benioff Children's Hospital, Oakland
Smilow Cancer Hospital, New Haven
Hackensack University Medical Center, Hackensack
Ottawa Hospital Research Institute, Ottawa
Princess Margaret Cancer Centre, Toronto
Centre Hospitalier Universitaire Sainte-Justine, Montreal
Lead Sponsor
Editas Medicine, Inc.
INDUSTRY