Evaluating the Pharmacokinetics, Pharmacodynamics, and Safety of Efgartigimod Administered Intravenously in Children With Generalized Myasthenia Gravis

PHASE2/PHASE3RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

October 26, 2021

Primary Completion Date

March 31, 2027

Study Completion Date

March 31, 2027

Conditions
Generalized Myasthenia Gravis
Interventions
BIOLOGICAL

Efgartigimod IV

Intravenous infusion of Efgartigimod

Trial Locations (24)

121

COMPLETED

Vian - M. Iashvili Children's Central Hospital, Tbilisi

159

COMPLETED

Tbilisi State Medical University - Givi Zhvania Pediatric Academic Clinic, Tbilisi

1090

WITHDRAWN

Medizinische Universitat Wien, Vienna

2650

RECRUITING

Universitair Ziekenhuis Antwerpen, Antwerp

13353

COMPLETED

Charite Universitaetsmedizin Berlin - Campus Virchow-Klinikum - Sozialpadiatrisches Zentrum, Berlin

13385

RECRUITING

AP-HM - Hopital de la Timone, Marseille

16147

RECRUITING

Ospedale Giannina Gaslini, Genova

22903

RECRUITING

University of Virginia (UVA) Health - Developmental Pediatrics Clinic, Charlottesville

27599

RECRUITING

University of North Carolina at Chapel Hill, Chapel Hill

45147

COMPLETED

Universitätsklinikum Essen, Essen

46026

RECRUITING

Hospital Universitari i Politecnic La Fe de Valencia, Valencia

50139

RECRUITING

Azienda Ospedaliero Universitaria A. Meyer, Florence

60611

RECRUITING

Ann and Robert H Lurie Children's Hospital of Chicago - Main Hospital, Chicago

70124

RECRUITING

Azienda Ospedaliera Universitaria Policlinico Consorziale Di Bari, Bari

75015

RECRUITING

Assistance Publique Hopitaux de Paris (AP-HP) - Hopital Necker-Enfants Malades, Paris

V6H 3N1

RECRUITING

British Columbia Children's Hospital, Vancouver

2333 ZA

RECRUITING

Leids Universitair Medisch Centrum, Leiden

80-952

RECRUITING

Uniwersyteckie Centrum Kliniczne, Gdansk

40-123

RECRUITING

Wielospecjalistyczna Poradnia Lekarska Synapsis, Katowice

02-097

RECRUITING

Centralny Szpital Kliniczny - Uniwersyteckie Centrum Kliniczne WUM, Warsaw

08950

RECRUITING

Hospital Sant Joan de Deu, Esplugues de Llobregat

WC1N 3JH

RECRUITING

Great Ormand Street Hospital for Children NHS Foundation Trust - Great Ormond Street Hospital, London

M13 9WL

RECRUITING

Manchester University NHS Foundation Trust - Royal Manchester Children's Hospital, Manchester

OX3 9DU

RECRUITING

Oxford University Hospitals NHS Foundation Trust - John Radcliffe Hospital Children's Hospital, Oxford

Sponsors

Lead Sponsor

All Listed Sponsors
lead

argenx

INDUSTRY

NCT04833894 - Evaluating the Pharmacokinetics, Pharmacodynamics, and Safety of Efgartigimod Administered Intravenously in Children With Generalized Myasthenia Gravis | Biotech Hunter | Biotech Hunter