Safety, Efficacy and PK of BIVV001 in Pediatric Patients With Hemophilia A

PHASE3CompletedINTERVENTIONAL
Enrollment

74

Participants

Timeline

Start Date

February 19, 2021

Primary Completion Date

January 18, 2023

Study Completion Date

January 18, 2023

Conditions
Hemophilia A
Interventions
DRUG

efanesoctocog alfa (BIVV001)

Pharmaceutical form: solution for injection Route of administration: IV

Trial Locations (40)

402

Investigational Site Number :1580001, Taichung

407

Investigational Site Number :1580003, Taichung

2145

Investigational Site Number :0360001, Westmead

4101

Investigational Site Number :0360002, South Brisbane

7623

Investigational Site Number :3480005, Pécs

8032

Investigational Site Number :7560001, Zurich

10002

Investigational Site Number :1580002, Taipei

10021

NY Presbyterian - Weill Cornell Medical Center-Site Number:8400020, New York

11031

Investigational Site Number :1580004, Taipei

20121

Investigational Site Number :3800001, Milan

20502

Investigational Site Number :7520001, Malmo

27834

East Carolina University/Brody Medical Sciences Building-Site Number:8400015, Greenville

28046

Investigational Site Number :7240001, Madrid

30322

Children's Healthcare of Atlanta-Site Number:8400019, Atlanta

32610

University of Florida-Site Number:8400009, Gainesville

34390

Investigational Site Number :7920001, Istanbul

43205

Childrens Hospital Of Columbus-Site Number:8400012, Columbus

45206

Cincinnati Children's Hospital Medical Center-Site Number:8400008, Cincinnati

52242

University of Iowa Hospitals and Clinics-Site Number:8400002, Iowa City

59037

Investigational Site Number :2500003, Lille

60590

Investigational Site Number :2760001, Frankfurt am Main

69500

Investigational Site Number :2500004, Bron

80123

Investigational Site Number :3800002, Napoli

80337

Investigational Site Number :2760002, München

90027

Children's Hospital Los Angeles-Site Number:8400006, Los Angeles

94275

Investigational Site Number :2500001, Le Kremlin-Bicêtre

60612-3833

Rush University Medical Center-Site Number:8400001, Chicago

53226-0509

Children's Hospital Of Wisconsin-Site Number:8400005, Milwaukee

L8N 3Z5

Investigational Site Number :1240004, Hamilton

N6A 4G5

Investigational Site Number :1240003, London

K1H 8L1

Investigational Site Number :1240002, Ottawa

M5G 1X8

Investigational Site Number :1240001, Toronto

D12 N512

Investigational Site Number :3720001, Dublin

1105 AZ

Investigational Site Number :5280002, Amsterdam

3584 CX

Investigational Site Number :5280001, Utrecht

08950

Investigational Site Number :7240002, Esplugues de Llobregat

07059

Investigational Site Number :7920004, Antalya

TR-35100

Investigational Site Number :7920003, Izmir

B4 6NH

Investigational Site Number :8260003, Birmingham

WC1N3JH

Investigational Site Number :8260001, London

All Listed Sponsors
lead

Bioverativ, a Sanofi company

INDUSTRY

NCT04759131 - Safety, Efficacy and PK of BIVV001 in Pediatric Patients With Hemophilia A | Biotech Hunter | Biotech Hunter